How much do you know about gene therapy?

Test your knowledge with the questions below!

1. What is the goal of gene therapy?

  • Slow or stabilize a disease
  • Protect a person from developing a disease

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2. A genetic disease may be caused by a gene mutation. This may result in not enough of an important ________ being made. What word is missing in the previous sentence?

  • DNA
  • Gene
  • Protein
  • Cell

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3.The three main components of a gene therapy are: vector, promoter, and ________?

  • DNA
  • Protein
  • Cell
  • Transgene

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4. True or false? All gene therapies utilize the same vector, promoter, and transgene.

  • True
  • False

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5. Which of the following statements is incorrect?

  • The vector aims to deliver the promoter and transgene to target cells
  • The promoter aims to turn on the transgene no matter where in the body the transgene is
  • The transgene contains the information to tell the body to make a new protein
  • The goal of the new protein is to replace or restore an important job in the body with the goal of slowing or stabilizing a disease

[click to highlight correct answer]


Do you have gene therapy science questions that you would like addressed in future GT 101 chapters?
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